Pioneering stem cell/gene therapy trials
Author(s)
Bibliographic Information
Pioneering stem cell/gene therapy trials
（Progress in gene therapy, v. 2）
VSP, 2004
Available at 2 libraries
Note
Includes bibliographical references and index
Description and Table of Contents
Description
The first unequivocal success for Gene Therapy was reported in April 2000 for X-SCID patients. Pioneering stem cell/gene therapy clinical trials are the focus of this book. Therapy successes such as the X-SCID trial and improved ADA-SCID ones are presented together with pioneering angio/vasculogenic clinical trials mediated either by transient gene therapy or emerging autologous stem cell transplantation. Highlights also include 1) promises of the breakthrough combination of stem cell- and transient gene-therapy, 2) gene therapy trials for neurodegenerative disease on non-human primates where long-term gene therapy might involve brain stem cells, and 3) the first clinical trial with non-invasive monitoring of therapeutic gene expression as a prospective conclusion.
This volume will be of value and interest to researchers in this exciting field.
by "Nielsen BookData"